T Y Alvin Liu,Neil M Bressler
T Y Alvin Liu
Vision Outcomes in Children Treated With Voretigene Neparvovec for RPE65-Associated Retinopathy [0.03%]
RPE65相关性视网膜病接受Voretigene Neparvovec治疗的儿童远期视觉转归分析
Dorothy A Thompson,Elisabeth De Smit,Weijen Tan et al.
Dorothy A Thompson et al.
Importance: Voretigene neparvovec (VN) marketed as Luxturna (Novartis Europharm Ltd) is the first approved gene therapy for severe RPE65-related retinal dystrophy, showing low-luminance vision improvement in adult trials....
Tomas S Aleman,Artur V Cideciyan
Tomas S Aleman
Phenotypic Manifestations in Female Carriers of RPGR ORF15 Variants Causing X-Linked Cone Dystrophy [0.03%]
RPGRorf15变异型X连锁视锥营养不良的女性携带者的表型表现
Shabnam Raji,Robert Edward MacLaren,Peter Charbel Issa et al.
Shabnam Raji et al.
Importance: Recent insights into impaired glutamylation caused by distal truncating variants in RPGR ORF15 and its association with the cone-dominated phenotype have provided the first molecular evidence of a genotype-phe...
Siri D,Manasi Tripathi,Arnav Panigrahi
Siri D
Emily S Wong,Richard W Choy,Yuzhou Zhang et al.
Emily S Wong et al.
Importance: Retinopathy of prematurity (ROP) is a leading cause of childhood blindness, particularly in low- and middle-income countries. With advancements in neonatal care, a projected rising trend and burden of ROP-rela...
The Global Epidemiologic Transition of Retinopathy of Prematurity: Interpreting Forecasts Through a Health-System Lens [0.03%]
早产儿视网膜病变的全球流行病学转变：通过卫生系统视角解读预测模型
Thanitsara Rittiphairoj
Thanitsara Rittiphairoj
Elizabeth Rooks,Samson Darrah,Behrouz Rahimi et al.
Elizabeth Rooks et al.
Aflibercept 8 mg in Polypoidal Choroidal Vasculopathy: Post Hoc Analysis of the PULSAR Randomized Clinical Trial [0.03%]
阿柏西普8mg治疗脉络膜新生血管的疗效分析——PULSAR随机临床试验的事后分析
Won Ki Lee,Tien Y Wong,Shih-Jen Chen et al.
Won Ki Lee et al.
Importance: In the Study of the Effects of High-Dose Aflibercept Injected Into the Eye of Patients With an Age-Related Disorder That Causes Loss of Vision Due to Growth of Abnormal Blood Vessels at the Back of the Eye (PU...
Voraporn Chaikitmongkol
Voraporn Chaikitmongkol