Safety and efficacy of levacetylleucine in ataxia-telangiectasia: a phase 3, randomised, double-blind, placebo-controlled crossover trial [0.03%]
左乙酰半胱氨酸治疗共济基管扩张症的疗效和安全性:一项随机、双盲、安慰剂对照交叉试验
Kyriakos Martakis,Tatiana Bremova-Ertl,Clare Bolton et al.
Kyriakos Martakis et al.
Background: Ataxia-telangiectasia is a rare, autosomal recessive neurodegenerative disorder. Levacetylleucine (N-acetyl-L-leucine) has been shown to be efficacious for the treatment of neurological manifestations and to h...
Clinical Trial
The Lancet. Neurology. 2026 Jul;25(7):633-644. DOI:10.1016/S1474-4422(26)00158-4 2026
Robert Stirrups
Robert Stirrups
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Kazutoshi Takahashi
Jules Morgan
Jules Morgan
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optic nerve involvement in multiple sclerosis诊断中的optic nerve involvement - 作者回复
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Shiv Saidha et al.
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