Treating SOD1-ALS with tofersen results in nonprogressive chronic ALS-a case series from Iceland
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Amyotrophic lateral sclerosis (ALS) is a progressive neurodegenerative disorder. We describe four patients with hereditary ALS caused by the p.Gly94Ser SOD1 mutation who were treated monthly with the intrathecal antisense oligonucleotide tofersen in a clinical... ...
