Signal transduction and targeted therapy. 2025 Feb 17;10(1):55. doi: 10.1038/s41392-025-02135-9 Q140.82024
Successful treatment of transfusion-dependent β-thalassemia: multiple paths to reach potential cure
成功治疗输血依赖性β-地中海贫血:通向潜在治愈的多种路径 翻译改进
Michael Morgan 1 2, Axel Schambach 3 4 5
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作者单位
1 Institute of Experimental Hematology, Hannover Medical School, Hannover, 30625, Germany.2 REBIRTH Research Center for Translational Regenerative Medicine, Hannover Medical School, Hannover, 30625, Germany.3 Institute of Experimental Hematology, Hannover Medical School, Hannover, 30625, Germany. schambach.axel@mh-hannover.de.4 REBIRTH Research Center for Translational Regenerative Medicine, Hannover Medical School, Hannover, 30625, Germany. schambach.axel@mh-hannover.de.5 Division of Hematology / Oncology, Boston Children's Hospital, Harvard Medical School, Boston, MA, 02115, USA. schambach.axel@mh-hannover.de.
DOI: 10.1038/s41392-025-02135-9 PMID: 39956809
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