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Patisiran in ATTRv amyloidosis with polyneuropathy: "PatisiranItaly" multicenter observational study

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Background: Hereditary amyloid transthyretin amyloidosis with polyneuropathy (ATTRv-PN) is a rare, inherited, multisystemic, progressive adult-onset disease, affecting sensorimotor nerves, and various organs. It is caused by muta... ...