PCDH15 dual-AAV gene therapy for deafness and blindness in Usher syndrome type 1F models
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Usher syndrome type 1F (USH1F), resulting from mutations in the protocadherin-15 (PCDH15) gene, is characterized by congenital lack of hearing and balance, and progressive blindness in the form of retinitis pigmentosa. In this study, we explore an approach for... ...
