Subretinal gene therapy delays vision loss in a Bardet-Biedl Syndrome type 10 mouse model
{{output}}
Blindness in Bardet-Biedl syndrome (BBS) is caused by dysfunction and loss of photoreceptor cells in the retina. BBS10, mutations of which account for approximately 21% of all BBS cases, encodes a chaperonin protein indispensable for the assembly of the BBSome... ...
